Gene Therapy Improves Vision in hereditary blindness: Study Finds Dr. Garima Soni12 Sept 2024 7:45 AM ISTBothnia dystrophy is a form of hereditary blindness that leads to progressive visual impairment due to the destruction of the visual cells in the...
Gene therapy restores vision in first-ever trial for rare, inherited blindness finds Lancet study Dr. Kamal Kant Kohli7 Sept 2024 7:15 AM ISTAfter the treatment, one patient saw her first star. Another saw snowflakes for the first time. Other patients were newly able to navigate outside of...
Carbonic Anhydrase Inhibitors Show Promise for X-Linked Retinoschisis, suggests study Dr Riya Dave5 July 2024 8:00 PM ISTResearchers have found that carbonic anhydrase inhibitors (CAIs) may offer beneficial short-term management for cystoid fluid collections (CFC) in...
FDA Expands Approval of Gene Therapy for Patients with Duchenne Muscular Dystrophy Dr. Kamal Kant Kohli22 Jun 2024 7:45 AM ISTThe U.S. Food and Drug Administration expanded the approval of Elevidys (delandistrogene moxeparvovec-rokl), a gene therapy for the treatment of...
Study suggests promising gene therapy for FOXG1 syndrome Dr. Kamal Kant Kohli16 Jun 2024 8:15 PM ISTA viral gene therapy developed by University at Buffalo researchers has reversed some brain abnormalities in infant mice with FOXG1 syndrome, a...
FDA fast tracks investigational gene therapy for heart failure Dr. Kamal Kant Kohli24 April 2024 7:30 PM ISTThe US Food and Drug Administration (FDA) has granted Fast Track designation to invesigational gene therapy AB-1002 for treatment of congestive heart...
Scientists discover potential treatment approaches for polycystic kidney disease Dr. Kamal Kant Kohli20 April 2024 6:45 AM ISTResearchers have shown that dangerous cysts, which form over time in polycystic kidney disease (PKD), can be prevented by a single normal copy of a...
FIRST: President of India unveils India's home-grown gene therapy for cancer Ruchika Sharma5 April 2024 11:30 AM ISTThe President was happy to note that the therapy being launched is the world's most affordable CAR-T cell therapy.
Experimental gene therapy for giant axonal neuropathy promising in clinical trial: NEJM Dr. Kamal Kant Kohli21 March 2024 8:45 PM ISTAn investigational gene therapy for a rare neurodegenerative disease that begins in early childhood, known as giant axonal neuropathy (GAN), was well...
Gene therapy restores hearing in children with hereditary deafness Dr. Kamal Kant Kohli25 Jan 2024 4:23 PM ISTA new study co-led by investigators from Mass Eye and Ear, a member of Mass General Brigham, demonstrated the effectiveness of a gene therapy towards...
Pfizer gene therapy for bleeding disorder approved in Canada Ruchika Sharma4 Jan 2024 11:51 AM ISTCanada: Pfizer said on Wednesday that Canada's health regulator approved its gene therapy for the treatment of a rare inherited bleeding...
Cell, gene therapy to rule pharma sector in 2024: Report MD Bureau29 Dec 2023 11:30 AM ISTThe report estimates that the global CGT market is projected to reach $80 billion by 2029.
