Insud Pharma inaugrates Oligonucleotides Centre in India Ruchika Sharma17 Sep 2023 7:30 AM GMTThis new plant will be capable of producing a novel antisense Oligonucleotide for the treatment of Spinal Muscular Atrophy.
Roche Evrysdi gets CHMP recommendation for babies under two months old with spinal muscular atrophy Ruchika Sharma24 July 2023 10:00 AM GMTEvrysdi is currently approved in the EU for the treatment of patients aged two months or older,
Kerala: Doctors at MCH perform spine surgery on 14-year-old SMA patient Kajal Rajput29 May 2023 7:30 AM GMTThiruvananthapuram: In a relief for Spinal Muscular Atrophy patients, a government medical college in Kerala has launched an innovative surgery to...
EMA seeks to issue guidance on liver damage from Novartis gene therapy Zolgensma Ruchika Sharma15 Jan 2023 6:45 AM GMTThe drug won conditional EU approval during early 2020 and it costs more than $2 million per patient
Zolgensma gene therapy caused two fatalities from liver failure, reports Novartis Ruchika Sharma14 Aug 2022 8:30 AM GMTBasel: Novartis AG on Thursday reported two patient fatalities due to acute liver failure following treatment with Zolgensma gene therapy used to...
Novartis donates Rs 16 crore drug to 23 month old Spinal Muscular Atrophy Type 1 patient MD Bureau8 Aug 2022 10:46 AM GMTAccording to Praveen, they had registered their daughter under Managed Access Programme of Novartis and they received the information that the company...
Roche gets USFDA nod for spinal muscular atrophy therapy Evrysdi for babies below 2 months Ruchika Sharma31 May 2022 10:32 AM GMTOf the babies with 2 or 3 copies of the SMN2 gene (n=6), 100% were able to sit after one year of treatment with Evrysdi, 67% could stand and 50% of...
Once-Daily Risdiplam beneficial in patients with Types 2 and 3 SMA: Lancet Dr. Shravani Dali19 Jan 2022 3:30 AM GMTOnce-Daily Risdiplam is beneficial in patients with Types 2 and 3 spinal muscular atrophy (SMA), according to a recent study published in the Lancet....
Submit interim safety report: CDSCO panel tells Novartis for phase 3 study of intrathecal OAV-101 Medical Dialogues Team7 Nov 2021 4:00 AM GMTNew Delhi: In a significant development, drug firm Novartis has got a green signal from the Subject Expert Committee (SEC) functional under the...
One-year-old Pune girl who received Rs 16 crore injection for Spinal Muscular Atrophy dies Medical Dialogues Bureau3 Aug 2021 3:30 AM GMTHer rare ailment and the quest for treatment had created a huge impact on social media with netizens and others donating an amount of Rs 14 crore,...
FIRST: Roche launches Spinal Muscular Atrophy treatment Evrysdi in India Ruchika Sharma30 July 2021 8:00 AM GMTMumbai: Roche has announced the launch of Evrysdi (risdiplam), the first and only approved treatment in India for Spinal Muscular Atrophy (SMA)...
Kerala HC stresses Govt control over crowdfunding after family raises Rs 18 crore for treatment of rare disease Medical Dialogues Bureau11 July 2021 4:15 AM GMT"I do not want every Tom, Dick and Harry to collect money. Is there any state control over this collection of funds via crowdfunding? We should know...
