USFDA Approves Roche's Evrysdi Tablet for Spinal Muscular Atrophy Farhat Nasim15 Feb 2025 10:45 AM ISTEvrysdi is the only non-invasive disease-modifying treatment for SMA.
Medical Bulletin 04 January/ 2025 Dr. Bhumika Maikhuri4 Jan 2025 3:00 PM ISTHere are the top medical news for the dayUnderstanding Duchenne Muscular Dystrophy: Study Unveils Critical Protein Interactions A new study has shed...
Study Highlights Critical Protein Interactions In Duchenne Muscular Dystrophy Dr. Bhumika Maikhuri4 Jan 2025 8:00 AM ISTA new study has shed light on the complex interactions between dystrophin, a protein critical to muscle stability, and its partner protein,...
Research finds New drug promising against Duchenne muscular dystrophy Dr. Kamal Kant Kohli17 Dec 2024 9:00 PM ISTA novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle degeneration. McGill...
FDA Expands Approval of Gene Therapy for Patients with Duchenne Muscular Dystrophy Dr. Kamal Kant Kohli22 Jun 2024 7:45 AM ISTThe U.S. Food and Drug Administration expanded the approval of Elevidys (delandistrogene moxeparvovec-rokl), a gene therapy for the treatment of...
FDA Approves novel Treatment for Duchenne Muscular Dystrophy Dr. Kamal Kant Kohli22 March 2024 3:30 PM ISTDuchenne Muscular Dystrophy is a rare neurological disorder of children which causes progressive muscle weakness due to a lack of muscle protein...
No custom duty on medicines for rare diseases: Delhi HC IANS5 March 2024 12:55 PM ISTThe court has directed customs authorities to prioritise and expedite the clearance of such medical imports, ensuring that treatments reach patients...
Aurobindo Pharma bags USFDA okay for Duchenne muscular dystrophy drug Deflazacort Ruchika Sharma13 Feb 2024 11:59 AM ISTHyderabad: Aurobindo Pharma Limited has announced that the Company has received final approval from the US Food & Drug Administration...
Sarepta says its experimental Duchenne drug more effective than older medicine Kajal Rajput30 Jan 2024 11:30 AM ISTNew Delhi: Sarepta Therapeutics' experimental drug produced higher levels of a specific protein deficient in some patients with Duchenne muscular...
FDA gives nod to novel steroid for treatment of Duchenne muscular dystrophy Dr. Kamal Kant Kohli29 Oct 2023 10:00 PM ISTThe US Food and Drug Administration has approved Vamorolone (Agamree), a novel corticosteroid for treatment of Duchenne muscular dystrophy (DMD) in...
Gene therapy receives FDA approval for Duchenne Muscular Dystrophy Medha Baranwal24 Jun 2023 10:00 AM ISTUSA: The U.S. Food and Drug Administration (FDA) has approved delandistrogene moxeparvovec (Elevidys), the first gene therapy for children 4 through 5...
Delhi HC sets up 5 member panel to implement rare disease policy Kajal Rajput31 May 2023 9:30 AM ISTNew Delhi: The Delhi High Court has constituted a five-member committee to implement the rare diseases policy formulated by the Central...
