Ranicel found effective in transfusions dependent beta thalassemia in phase 1/2 clinical trial Dr. Kamal Kant Kohli17 Jun 2024 8:45 PM ISTRenizgamglogene autogedtemcel (reni-cel), formerly known as EDIT-301 has demonstrated promising effect in the treatment of transfusion-dependent...
Rare Disease Show: Episode 3 Understanding Thallasemia with Dr Anupam Sachdeva Dr. Nandita Mohan28 May 2024 9:30 AM ISTMedical Dialogues presents a rare disease series, delving into the realm of uncommon medical conditions. Rare diseases are medical conditions that...
Bristol Myers Squibb Reblozyl gets European Commission nod for anemia due to Beta Thalassemia Ruchika Sharma5 March 2023 11:30 AM ISTReblozyl, a first-in-class therapeutic option, promotes late-stage red blood cell maturation in animal models.
Post USFDA nod, Bluebird Bio USD 2.8 million gene therapy becomes most expensive drug Ruchika Sharma19 Aug 2022 4:32 PM ISTBluebird has pitched Zynteglo as a potential one-time treatment that could do away with the need for transfusions, resulting in savings for patients...
USFDA panel backs Bluebird bio gene therapy for blood disorder Ruchika Sharma12 Jun 2022 12:00 PM ISTThe FDA is expected to decide on beti-cel's fate by Aug. 19 and eli-cel's by Sept. 16. The agency is not required to follow its advisers'...
Bristol Myers Squibb withdraws supplemental biologics license application for Reblozyl for Non-transfusion Dependent (NTD) Beta Thalassemia Ruchika Sharma5 Jun 2022 5:00 PM ISTReblozyl, a first-in-class therapeutic option, is currently approved in the United States, European Union and Canada to address transfusion-dependent...
Gene therapy effective in beta-thalassemia, reduces need for transfusion: NEJM Medha Baranwal1 Jan 2022 9:00 AM ISTUSA: A phase III study showed betibeglogene autotemcel (beti-cel) gene therapy to be safe and effective in patients with non-β0/β0 genotype...
Frame guidelines on thalassemia treatment: SC to Centre savita thakur thakur31 Jan 2018 9:30 AM ISTNew Delhi: The Supreme Court asked the Centre to come up with guidelines for providing treatment to patients suffering from Thalassemia within four...
