Topical gene therapy promising for complete wound healing in dystrophic epidermolysis bullosa patients: NEJM Medha Baranwal15 Dec 2022 2:30 PMUSA: Dystrophic epidermolysis bullosa is a genetic skin disorder that causes the skin to be fragile and blister easily. Mutations in COL7A1 that...
World's most expensive drug: USFDA nod to HEMGENIX worth USD 3.5 million a dose Roshni Dhar25 Nov 2022 12:11 PMGlobal biotechnology leader CSL has announced that the U.S. Food and Drug Administration (USFDA) has approved HEMGENIX (etranacogene...
Health Bulletin 25/November/2022 Roshni Dhar25 Nov 2022 11:21 AMHere are the top health news for the day:Thirteen measles deaths reported in Mumbai An eight-year-old boy from Govandi died on Thursday due to...
First gene therapy for hemophilia B treatment receives FDA approval Dr. Kamal Kant Kohli23 Nov 2022 2:30 PMUSA: Hemgenix, an adeno-associated virus vector-based gene therapy, has received approval from the U.S. Food and Drug Administration (FDA) for the...
Gene therapy for rare blinding disease of children developed by NIH researchers Dr. Kamal Kant Kohli13 Sept 2022 2:00 PMResearchers from the National Eye Institute (NEI) have developed a gene therapy for rare blinding disease of children. The therapy rescues cilia...
Novel gene therapy for rare ciliopathy Isra Zaman9 Sept 2022 4:00 AMResearchers from the National Eye Institute have developed a gene therapy that rescues cilia defects in retinal cells affected by a type of Leber...
Medical Bulletin 31/August/2022 Isra Zaman31 Aug 2022 9:39 AMHere are the top medical news for the day:Second breast cancer risk highlighted by Breast MRIAccording to a study that was published in Radiology, a...
Post USFDA nod, Bluebird Bio USD 2.8 million gene therapy becomes most expensive drug Ruchika Sharma19 Aug 2022 11:02 AMBluebird has pitched Zynteglo as a potential one-time treatment that could do away with the need for transfusions, resulting in savings for patients...
Zolgensma gene therapy caused two fatalities from liver failure, reports Novartis Ruchika Sharma14 Aug 2022 8:30 AMBasel: Novartis AG on Thursday reported two patient fatalities due to acute liver failure following treatment with Zolgensma gene therapy used to...
Novartis donates Rs 16 Crore gene therapy to 23 month old Spinal Muscular Atrophy Type 1 patient Roshni Dhar9 Aug 2022 12:30 PMA 23-month-old baby with Spinal Muscular Atrophy (SMA) Type 1, received a new lease of life with Swiss drugmaker Novartis coming forward to donate...
Health Bulletin 9/ August/ 2022 Roshni Dhar9 Aug 2022 11:57 AMHere are the Top Health stories for the day:Telangana baby with rare genetic disease administered Rs 16 crore drugA 23-month-old baby with Spinal...
Novartis donates Rs 16 crore drug to 23 month old Spinal Muscular Atrophy Type 1 patient MD Bureau8 Aug 2022 10:46 AMAccording to Praveen, they had registered their daughter under Managed Access Programme of Novartis and they received the information that the company...
