Novel gene therapy for rare ciliopathy Isra Zaman9 Sept 2022 9:30 AM ISTResearchers from the National Eye Institute have developed a gene therapy that rescues cilia defects in retinal cells affected by a type of Leber...
Medical Bulletin 31/August/2022 Isra Zaman31 Aug 2022 3:09 PM ISTHere are the top medical news for the day:Second breast cancer risk highlighted by Breast MRIAccording to a study that was published in Radiology, a...
Post USFDA nod, Bluebird Bio USD 2.8 million gene therapy becomes most expensive drug Ruchika Sharma19 Aug 2022 4:32 PM ISTBluebird has pitched Zynteglo as a potential one-time treatment that could do away with the need for transfusions, resulting in savings for patients...
Zolgensma gene therapy caused two fatalities from liver failure, reports Novartis Ruchika Sharma14 Aug 2022 2:00 PM ISTBasel: Novartis AG on Thursday reported two patient fatalities due to acute liver failure following treatment with Zolgensma gene therapy used to...
Novartis donates Rs 16 Crore gene therapy to 23 month old Spinal Muscular Atrophy Type 1 patient Roshni Dhar9 Aug 2022 6:00 PM ISTA 23-month-old baby with Spinal Muscular Atrophy (SMA) Type 1, received a new lease of life with Swiss drugmaker Novartis coming forward to donate...
Health Bulletin 9/ August/ 2022 Roshni Dhar9 Aug 2022 5:27 PM ISTHere are the Top Health stories for the day:Telangana baby with rare genetic disease administered Rs 16 crore drugA 23-month-old baby with Spinal...
Novartis donates Rs 16 crore drug to 23 month old Spinal Muscular Atrophy Type 1 patient MD Bureau8 Aug 2022 4:16 PM ISTAccording to Praveen, they had registered their daughter under Managed Access Programme of Novartis and they received the information that the company...
Hope for treatments against hearing loss as 10 genes identified Dr. Kamal Kant Kohli26 May 2022 8:45 PM ISTResearchers led by King's College London, Karolinska Institute and Erasmus University have identified 10 new genes linked with hearing loss and...
Gene therapy shows promise in treating neuropathy from spinal cord injuries Dr. Kamal Kant Kohli17 May 2022 10:30 AM ISTAn international team of researchers, led by scientists at University of California San Diego School of Medicine, report that a gene therapy that...
Gene therapy effective in beta-thalassemia, reduces need for transfusion: NEJM Medha Baranwal1 Jan 2022 9:00 AM ISTUSA: A phase III study showed betibeglogene autotemcel (beti-cel) gene therapy to be safe and effective in patients with non-β0/β0 genotype...
Gene Therapy Shows Early Promise as Angelman Syndrome Treatment Hina Zahid28 Oct 2021 9:00 AM ISTCHAPEL HILL, NC - Angelman syndrome, a neurodevelopmental disorder that features poor muscle control and balance, hard-to-treat epilepsy, and...
Pfizer, Voyager Therapeutics ink USD 630 million gene therapy deal Medical Dialogues Team10 Oct 2021 9:45 AM ISTUnder the terms of the agreement, Pfizer will have the right to evaluate novel capsids selected for central nervous system and cardiac tropisms from...
